Introduction

Australia and New Zealand are rapidly cementing their position as regional leaders in biologics, cell & gene therapy (CGT), and RNA innovation. With world-class research institutes, strong clinical trial infrastructure, and active biotech ecosystems, the ANZ region continues to attract global attention for its early-stage and translational development strength.

This eBook highlights 10 of the most promising Phase 1 and 2 programmes driving therapeutic breakthroughs from next-generation CAR-T and NK cell therapies to mRNA and RNA-editing platforms that are reshaping how we approach complex diseases.